CI

At a glance

ClinicalIndex Comparison Record
Phase 2Recruiting· 30 target
Drug / intervention
Ivosidenib +1 moredrug
Likely dose
Not stated in record
Key inclusion· 9
  • ECOG performance status 0-2
  • IDH1-R132 mutated disease confirmed by local lab
  • Treatment naive or relapsed/refractory AML eligible for intensive chemotherapy
  • High-risk MDS (IPSS-R ≥4) or MPN (D-IPSS ≥3) may be eligible with PI discussion
Key exclusion· 13
  • Prior CPX-351 therapy
  • Uncontrolled clinically significant medical condition including infection, lab abnormality, or psychiatric illness
  • Other chemotherapeutic or anti-leukemic agents during study (except intrathecal prophylaxis, controlled CNS leukemia, hydroxyurea, or limited cytarabine ≤2 g/m²)
  • Active GVHD post-stem cell transplant (stable/no active GVHD on chronic suppression permitted with PI discussion)

Standardized by ClinicalIndex from the ClinicalTrials.gov record · verify against the source.

Search/NCT04493164
NCT04493164Phase 2RecruitingOn Track
Long Recruiting

Phase II Investigator Sponsored Study of CPX-351 in Combination With Ivosidenib for Patients With IDH1 Mutated Acute Myeloid Leukemia or High-Risk MDS

M.D. Anderson Cancer Center·interventional·Posted Jul 30, 2020·Updated Jun 12, 2026

In Brief

A Phase 2 clinical trial evaluating Ivosidenib and Liposome-encapsulated Daunorubicin-Cytarabine for Acute Myeloid Leukemia With Gene Mutations and 4 related conditions. Currently recruiting, targeting 30 participants across 1 site.

Detailed Summary

This phase II trial investigates how well CPX-351 and ivosidenib work in treating patients with acute myeloid leukemia or high-risk myelodysplastic syndrome that has IDH1 mutation. The safety of this drug combination will also be studied. IDH1 is a type of genetic mutation (change). Chemotherapy drugs, such as CPX-351, work in different ways to stop the growth of cancer cells, either by killing the cells, by stopping them from dividing, or by stopping them from spreading. Ivosidenib may stop the growth of cancer cells by blocking some of the enzymes needed for cell growth. The purpose of this trial is to learn if CPX-351 in combination with ivosidenib can help to control IDH1-mutated acute myeloid leukemia or high-risk myelodysplastic syndrome.

Study Details

Study Typeinterventional
Allocation--
Masking--
Primary Purpose--
CountriesUnited States
Collaborators--

Timeline

Phase 2Recruiting
20212022202320242025202620272028
First PostedJul 30, 2020
Enrollment StartDec 30, 2020
Primary CompletionJun 1, 2028
TodayJul 1, 2026
Enrollment to primary: 7.4 yearsPosted 5.9 years agoPrimary completion in 1.9 years

Arms & Interventions

Treatment (CPX-351, ivosidenib)experimental

INDUCTION: Patients receive CPX-351 IV over 90 minutes on days 1, 3, and 5, and ivosidenib PO QD on days 1-28. Patients who do not achieve complete remission may receive a second cycle of induction therapy in the absence of disease progression or unacceptable toxicity. Patients achieving complete remission proceed to consolidation. CONSOLIDATION: Patients receive CPX-351 IV over 90 minutes on days 1 and 3, and ivosidenib PO QD on days 1-28. Treatment repeats every 28 days for up to 2 cycles in the absence of disease progression or unacceptable toxicity. MAINTENANCE: Patients receive ivosidenib PO QD for up to 2 years in the absence of disease progression or unacceptable toxicity. Patients who are experiencing clinical benefit and who have not experienced excessive toxicity after completion of 2 years of maintenance may be eligible to continue therapy after discussion with the principal investigator.

Drug: IvosidenibDrug: Liposome-encapsulated Daunorubicin-Cytarabine

Interventions

Ivosidenibdrug

Given PO

Liposome-encapsulated Daunorubicin-Cytarabinedrug

Given IV